Frequently Asked Questions
What is the purpose of this clinical research study?
The main purpose of this study is to determine whether the investigational medication used in this clinical research study will help shrink or delay the growth of your cancer.
How do I know if I am eligible?
You may be eligible to participate if:
You are a man or woman 18 years of age or older
You have been told by your doctor that you have advanced malignant perivascular epithelioid cell cancer or PEComa
The cancer may have been treated, but the disease has recurred or has gotten worse
You are able to walk and capable of non-strenuous physical activity
Other study criteria will be assessed at a screening visit.
How can I find-out more about participation in the study?
If you are interested in participating in the study the contact details of your nearest study center can be found by searching the study locations.
Is there a placebo (an inactive substance)?
No, there is no placebo used in this study. Everyone in this study receives the investigational medication.
Is this a blinded study or an open label study?
This study is not blinded, it is an open label study. This means that both participants and their study doctor will know which treatment patients are receiving.
What should I expect if I join the study?
You will be given information about the study and have the opportunity to ask questions, so that you can decide if you want to participate.
If you decide to take part in the study, you will sign the informed consent form which acknowledges your willingness to participate.
The study team will ask you to attend a screening visit to determine if your diagnosis is a good match for the study.
The amount of time patients will be in the study varies. You will remain in the study for as long as the study medication is of benefit to you or if you decide to withdraw from treatment. If you decide to stop treatment or the investigational medication is no longer of benefit, the next step in the study is to follow your condition overtime unless you decide to withdraw from any further participation in the study.
Taking part in this study may or may not improve your condition. There may be no benefit to you. There is a possibility that your condition may remain the same or get worse. There is also a possibility you will experience side effects, which may be serious, with the study medication. While you are in the study the study doctor will follow your condition closely.